Evrysdi treatment is safe and effective at improving or stabilizing motor and lung function in adults with SMA for up to 2 ...

Learn what you need to do to have a fun, safe, and stress-free day at an amusement park when you have spinal muscular atrophy.

Columnist Sherry Toh explains how her doctors demonstrated the correct way to provide a supportive environment for LGBTQ+ ...

A trip to England with her friend of 30-plus years prompts columnist Connie Chandler to give thanks for kind friends who ...

Early results obtained for the SMA patients demonstrated that, in those with elevated levels of neurofilament light chain (NfL), a marker of nerve cell damage, initiation of salanersen led to mean ...