ScienceAlert on MSN16h
Drug For Rare Disease Turns Human Blood Into Mosquito Poison
Scientists have a radical new plan for controlling mosquito numbers and fighting malaria: lacing human blood with a drug that ...
STAT11h
Soleno Therapeutics’ ‘life-changing’ rare-disease drug approved
The FDA Wednesday approved the first drug to treat people with Prader-Willi syndrome, a rare genetic disease that causes an ...
Dallas scientists granted $420K to test gene therapy for rare neurological disease
Childhood-onset striatonigral neurodegeneration robs children of the ability to walk and talk by age five. Researchers at ...
Rolling Out16h
5 ways AI and love conquered a deadly blood disorder
Machine learning and unwavering support helped Joseph Coates overcome POEMS syndrome. Discover how computational medicine is ...
Her Baby Had to Be Revived 8 Times in the NICU. Now She's Talking About His Rare Condition to Help Moms Like Her (Exclusive)
Cerebrocostomandibular syndrome is a rare genetic disorder characterized by a combination of abnormalities affecting the ...
To fight malaria, scientists want to poison mosquitos—with human blood
Low doses of a drug already approved for treating rare genetic conditions in humans kills mosquitoes dead. Scientists say it ...
Malaria breakthrough as scientists find drug makes human blood deadly to mosquitoes
Nitisinone was shown to last longer than ivermectin in the human bloodstream and was able to kill not only mosquitoes of all ...
BioPharma Dive21h
Epicrispr banks $68M to test epigenetic editing on rare muscle disease
The startup is using CRISPR tools to stop errant expression of a gene linked to facioscapulohumeral muscular dystrophy, a ...
LJ Smith dead: The Vampire Diaries author who inspired TV show dies after battle with rare disease
Author LJ Smith, who was behind the Vampire Diaries series that inspired the hit TV show of the same name, has died at the ...
BioPharma Dive12h
First Prader-Willi drug to reduce hunger approved by FDA
Clearance of Vykat unlocks what analysts anticipate will be a lucrative market opportunity for Soleno Therapeutics.
The Manila Times22h
Rezolute Announces Appointment of Rare Disease Commercial Leader Erik Harris to its Board of Directors
Mr. Harris is an experienced board member and commercial leader with a proven track record in the industry. Mr. Harris has spearheaded global product launches, built and led high-performing commercial ...
Drug treatment extended for Langford girl with rare fatal condition
The family of nine-year-old Charleigh Pollock will continue to be covered for the drug, which costs $1 million a year, until ...