Woman With Complex Congenital Heart Disease Receives World’s First Leadless Pacemaker Implant; Know How It Helps
In the rarest of rare cases and a groundbreaking medical achievement, Medica Superspecialty Hospital in Kolkata achieved a ...
Her Baby Had to Be Revived 8 Times in the NICU. Now She's Talking About His Rare Condition to Help Moms Like Her (Exclusive)
Cerebrocostomandibular syndrome is a rare genetic disorder characterized by a combination of abnormalities affecting the ...
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Soleno Therapeutics’ ‘life-changing’ rare-disease drug approved
The FDA Wednesday approved the first drug to treat people with Prader-Willi syndrome, a rare genetic disease that causes an ...
US FDA approves first treatment for rare genetic disorder Prader-Willi syndrome
The U.S. Food and Drug Administration on Wednesday approved Soleno Therapeutics' drug to treat a rare genetic disorder, ...
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First Prader-Willi drug to reduce hunger approved by FDA
Clearance of Vykat unlocks what analysts anticipate will be a lucrative market opportunity for Soleno Therapeutics.
US FDA greenlights first-ever treatment for rare genetic disorder
The U.S. Food and Drug Administration approved Soleno Therapeutics' drug to treat a rare genetic disorder on Wednesday, ...
To fight malaria, scientists want to poison mosquitos—with human blood
Low doses of a drug already approved for treating rare genetic conditions in humans kills mosquitoes dead. Scientists say it ...
Rolling Out15h
5 ways AI and love conquered a deadly blood disorder
Machine learning and unwavering support helped Joseph Coates overcome POEMS syndrome. Discover how computational medicine is ...
Rolling Out17h
Promising drug cuts Alzheimer’s risk by half in rare cases
Research shows experimental anti-amyloid drug reduced cognitive symptom risk by 50% in people with rare genetic mutations ...
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Epicrispr banks $68M to test epigenetic editing on rare muscle disease
The startup is using CRISPR tools to stop errant expression of a gene linked to facioscapulohumeral muscular dystrophy, a ...
Dallas scientists granted $420K to test gene therapy for rare neurological disease
Childhood-onset striatonigral neurodegeneration robs children of the ability to walk and talk by age five. Researchers at ...
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Hantavirus: Essential Information You Must Know About This Rare But Deadly Virus
One of the most serious complications is the build-up of fluid in the lungs, significantly hindering breathing. Without immediate medical intervention, hantavirus can lead to respiratory failure, with ...